Episode 59
Knowledge is Power: Part 2
Patient Empowerment Program: A Rare Disease Podcast
September 3, 202429m 34s
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Show Notes
The concluding episode of the Knowledge is Power series. The knowledge we are gaining at n-Lorem has even more value than benefiting nano-rare patients and their families. These insights will enable scientists to discover new therapeutic targets for both common and rare diseases, fundamentally changing the way we approach health and disease.
Survey – Patient Empowerment Program Podcast Register for the 2024 Nano-rare Patient Colloquium
Survey – Patient Empowerment Program Podcast Register for the 2024 Nano-rare Patient Colloquium
On This Episode We Discuss:
- Questions we can answer and teach us about health and disease and opportunities to treat more common diseases
- What are all the functions of human genes?
- Are there gene products that have redundant functions?
- Do identical mutations cause identical phenotypes?
- n-Lorem can demonstrate that ASOs work on general types of disease challenges